April 2023 - The Snow Foundation

The Snow Foundation is a Platinum Member of NORD

The Snow Foundation is proud to be a PLATINUM MEMBER of The National Organization of Rare Disorders. Check out their Website: https://rarediseases.org/

April 28, 2023/by The Snow Foundation

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Wolfram Syndrome Poster Presentation by Brianna Carman-Washington University School of Medicine-Urano Lab

April 25, 2023/by The Snow Foundation

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Febrile urinary tract infections common with neurogenic bladder

https://medicalxpress.com/news/2023-03-febrile-urinary-tract-infections-common.html

April 21, 2023/by The Snow Foundation

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Wolfram Syndrome Poster Presentation by William An and Megha Verma-Washington University School of Medicine-Urano Lab

April 18, 2023/by The Snow Foundation

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Amylyx Pharmaceuticals Announces First Participant Dosed in Phase 2 Study of AMX0035 for the Treatment of Wolfram Syndrome

https://www.amylyx.com/news/amylyx-pharmaceuticals-announces-first-participant-dosed-in-phase-2-study-of-amx0035-for-the-treatment-of-wolfram-syndrome

April 14, 2023/by The Snow Foundation

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The Ins and Outs of Gene Therapy for Inherited Optic Neuropathies

https://europe.ophthalmologytimes.com/view/the-ins-and-outs-of-gene-therapy-for-inherited-optic-neuropathies

(Image courtesy ©Fantastic / stock.adobe.com)

April 14, 2023/by The Snow Foundation

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Research

Amylyx Pharmaceuticals Announces First Participant Dosed in Phase 2 Study of AMX0035 for the Treatment of Wolfram Syndrome

Publication: Amylyx Pharmaceuticals, Inc. | Publication Date: April 13, 2023

Authors: Amylyx Pharmaceuticals, Inc.

Significance

Recently published preclinical data demonstrate initial proof-of-concept for the therapeutic development of AMX0035 (sodium phenylbutyrate and taurursodiol) in Wolfram syndrome

Read the entire research article here

April 13, 2023/by The Snow Foundation

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Wolfram Syndrome Poster Presentation by Nila Palaniappan-Washington University School of Medicine-Urano Lab

April 11, 2023/by The Snow Foundation

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Amylyx Pharmaceuticals Announces First Participant Dosed in Phase 2 Study of AMX0035 for the Treatment of Wolfram Syndrome

Significance

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