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Dr. Fumihiko Urano | Washington University School of Medicine, USA | Prilenia Therapeutics


Dr. Fumihiko Urano

Washington University School of Medicine, USA

Dear Friends,

Thank you sincerely for your invaluable support of our collaborative study alongside Prilenia Therapeutics. 

One promising candidate is the Sigma 1 receptor, and we have initiated a collaboration with Prilenia, a biotech company specializing in this field. Together, we are investigating the effects of a drug called pridopidine, which targets the Sigma 1 receptor, in cellular models of Wolfram syndrome. We are grateful to the Snow Foundation in collaboration with Ellie White Foundation for their generous donations, which enables us to conduct this crucial study using cells derived from Wolfram syndrome patients. The study is currently in progress as we explore various experimental conditions to assess the efficacy of pridopidine. We are committed to providing you with regular updates on our progress.

Once again, we extend our heartfelt thanks for your generous support, which is instrumental in advancing our mission to find a cure for Wolfram syndrome and bring hope to those affected by this condition.

With grace and gratitude,

Fumi

 

Fumihiko Urano, MD, PhD, FACMG

Professor of Medicine and of Pathology & Immunology

Samuel E. Schechter Endowed Professor in Medicine

Director, Wolfram Syndrome/WFS1-related disorders Registry & Clinical Study and WFS1 clinic at BJC HealthCare

Washington University School of Medicine

https://wolframsyndrome.wustl.edu/